Pharma & Healthcare

Global Hemophilia AAV Gene Therapy Market Research Report 2026

This report delivers a comprehensive overview of the global Hemophilia AAV Gene Therapy market, with both quantitative and qualitative analyses, to help readers develop growth strategies, assess the competitive landscape, evaluate their position in the current market, and make informed business decisions regarding Hemophilia AAV Gene Therapy. The Hemophilia AAV Gene Therapy market size, estimates, and forecasts are provided in terms of revenue (US$ millions), with 2025 as the base year and historical and forecast data for 2021–2032.
The report segments the global Hemophilia AAV Gene Therapy market comprehensively. Regional market sizes by Type, by Application, , and by player are also provided. For deeper insight, the report profiles the competitive landscape, key competitors, and their respective market rankings, and discusses technological trends and new product developments.
This report will assist Hemophilia AAV Gene Therapy manufacturers, new entrants, and companies across the industry value chain with information on revenues, sales volume, and average prices for the overall market and its sub-segments, by company, by Type, by Application, and by region.
Market Segmentation
By Company
BioMarin (Roctavian)
CSL/uniQure (Hemgenix&Glybera)
Pfizer
Segment by Type
AVV5 Vector
AAVrh74 Vector
Segment by Application
Hemophilia A
Hemophilia B
By Region
North America
U.S.
Canada
Asia-Pacific
China
Japan
South Korea
Southeast Asia
India
Australia & New Zealand
Rest of Asia
Europe
Germany
France
U.K.
Italy
Ireland
Russia
Rest of Europe
Latin America
Mexico
Brazil
Argentina
Rest of Latin America
Middle East & Africa
Israel
United Arab Emirates (UAE)
Saudi Arabia
Rest of MEA
Chapter Outline
Chapter 1: Defines the scope of the report and presents an executive summary of market segments (by Type, by Application, , etc.), including the size of each segment and its future growth potential. It offers a high-level view of the current market and its likely evolution in the short, medium, and long term.
Chapter 2: Summarizes global and regional market size and outlines market dynamics and recent developments, including key drivers, restraints, challenges and risks for industry participants, and relevant policy analysis.
Chapter 3: Provides a detailed view of the competitive landscape for Hemophilia AAV Gene Therapy companies, covering revenue share, development plans, and mergers and acquisitions.
Chapter 4: Analyzes segments by Type, detailing the size and growth potential of each segment to help readers identify blue-ocean opportunities.
Chapter 5: Analyzes segments by Application, detailing the size and growth potential of each downstream segment to help readers identify blue-ocean opportunities.
Chapter 6–10: Regional deep dives (North America, Europe, Asia Pacific, Latin America, Middle East & Africa) broken down by country. Each chapter quantifies market size and growth potential by region and key countries, and outlines market development, outlook, addressable space, and capacity.
Chapter 11: Profiles key players, presenting essential information on leading companies, including product/ service offerings, revenue, gross margin, product introductions/portfolios, recent developments, etc.
Chapter 12: Key findings and conclusions of the report.
1 Report Overview
1.1 Study Scope
1.2 Market Analysis by Type
1.2.1 Global Hemophilia AAV Gene Therapy Market Size Growth Rate by Type: 2021 vs 2025 vs 2032
1.2.2 AVV5 Vector
1.2.3 AAVrh74 Vector
1.3 Market by Application
1.3.1 Global Hemophilia AAV Gene Therapy Market Growth by Application: 2021 vs 2025 vs 2032
1.3.2 Hemophilia A
1.3.3 Hemophilia B
1.4 Assumptions and Limitations
1.5 Study Objectives
1.6 Years Considered
2 Global Growth Trends
2.1 Global Hemophilia AAV Gene Therapy Market Perspective (2021–2032)
2.2 Global Hemophilia AAV Gene Therapy Growth Trends by Region
2.2.1 Global Hemophilia AAV Gene Therapy Market Size by Region: 2021 vs 2025 vs 2032
2.2.2 Hemophilia AAV Gene Therapy Historic Market Size by Region (2021–2026)
2.2.3 Hemophilia AAV Gene Therapy Forecasted Market Size by Region (2027–2032)
2.3 Hemophilia AAV Gene Therapy Market Dynamics
2.3.1 Hemophilia AAV Gene Therapy Industry Trends
2.3.2 Hemophilia AAV Gene Therapy Market Drivers
2.3.3 Hemophilia AAV Gene Therapy Market Challenges
2.3.4 Hemophilia AAV Gene Therapy Market Restraints
3 Competition Landscape by Key Players
3.1 Global Top Hemophilia AAV Gene Therapy Players by Revenue
3.1.1 Global Top Hemophilia AAV Gene Therapy Players by Revenue (2021–2026)
3.1.2 Global Hemophilia AAV Gene Therapy Revenue Market Share by Players (2021–2026)
3.2 Global Top Hemophilia AAV Gene Therapy Players Market Share by Company Tier (Tier 1, Tier 2, Tier 3)
3.3 Global Key Players Ranking by Hemophilia AAV Gene Therapy Revenue
3.4 Global Hemophilia AAV Gene Therapy Market Concentration Ratio
3.4.1 Global Hemophilia AAV Gene Therapy Market Concentration Ratio (CR5 and HHI)
3.4.2 Global Top 10 and Top 5 Companies by Hemophilia AAV Gene Therapy Revenue in 2025
3.5 Global Key Players of Hemophilia AAV Gene Therapy Head Offices and Areas Served
3.6 Global Key Players of Hemophilia AAV Gene Therapy, Products and Applications
3.7 Global Key Players of Hemophilia AAV Gene Therapy, Date of General Availability (GA)
3.8 Mergers and Acquisitions, Expansion Plans
4 Hemophilia AAV Gene Therapy Breakdown Data by Type
4.1 Global Hemophilia AAV Gene Therapy Historic Market Size by Type (2021–2026)
4.2 Global Hemophilia AAV Gene Therapy Forecasted Market Size by Type (2027–2032)
5 Hemophilia AAV Gene Therapy Breakdown Data by Application
5.1 Global Hemophilia AAV Gene Therapy Historic Market Size by Application (2021–2026)
5.2 Global Hemophilia AAV Gene Therapy Forecasted Market Size by Application (2027–2032)
6 North America
6.1 North America Hemophilia AAV Gene Therapy Market Size (2021–2032)
6.2 North America Hemophilia AAV Gene Therapy Market Growth Rate by Country: 2021 vs 2025 vs 2032
6.3 North America Hemophilia AAV Gene Therapy Market Size by Country (2021–2026)
6.4 North America Hemophilia AAV Gene Therapy Market Size by Country (2027–2032)
6.5 United States
6.6 Canada
7 Europe
7.1 Europe Hemophilia AAV Gene Therapy Market Size (2021–2032)
7.2 Europe Hemophilia AAV Gene Therapy Market Growth Rate by Country: 2021 vs 2025 vs 2032
7.3 Europe Hemophilia AAV Gene Therapy Market Size by Country (2021–2026)
7.4 Europe Hemophilia AAV Gene Therapy Market Size by Country (2027–2032)
7.5 Germany
7.6 France
7.7 U.K.
7.8 Italy
7.9 Russia
7.10 Ireland
8 Asia-Pacific
8.1 Asia-Pacific Hemophilia AAV Gene Therapy Market Size (2021–2032)
8.2 Asia-Pacific Hemophilia AAV Gene Therapy Market Growth Rate by Region: 2021 vs 2025 vs 2032
8.3 Asia-Pacific Hemophilia AAV Gene Therapy Market Size by Region (2021–2026)
8.4 Asia-Pacific Hemophilia AAV Gene Therapy Market Size by Region (2027–2032)
8.5 China
8.6 Japan
8.7 South Korea
8.8 Southeast Asia
8.9 India
8.10 Australia & New Zealand
9 Latin America
9.1 Latin America Hemophilia AAV Gene Therapy Market Size (2021–2032)
9.2 Latin America Hemophilia AAV Gene Therapy Market Growth Rate by Country: 2021 vs 2025 vs 2032
9.3 Latin America Hemophilia AAV Gene Therapy Market Size by Country (2021–2026)
9.4 Latin America Hemophilia AAV Gene Therapy Market Size by Country (2027–2032)
9.5 Mexico
9.6 Brazil
10 Middle East & Africa
10.1 Middle East & Africa Hemophilia AAV Gene Therapy Market Size (2021–2032)
10.2 Middle East & Africa Hemophilia AAV Gene Therapy Market Growth Rate by Country: 2021 vs 2025 vs 2032
10.3 Middle East & Africa Hemophilia AAV Gene Therapy Market Size by Country (2021–2026)
10.4 Middle East & Africa Hemophilia AAV Gene Therapy Market Size by Country (2027–2032)
10.5 Israel
10.6 Saudi Arabia
10.7 UAE
11 Key Players Profiles
11.1 BioMarin (Roctavian)
11.1.1 BioMarin (Roctavian) Company Details
11.1.2 BioMarin (Roctavian) Business Overview
11.1.3 BioMarin (Roctavian) Hemophilia AAV Gene Therapy Introduction
11.1.4 BioMarin (Roctavian) Revenue in Hemophilia AAV Gene Therapy Business (2021–2026)
11.1.5 BioMarin (Roctavian) Recent Development
11.2 CSL/uniQure (Hemgenix&Glybera)
11.2.1 CSL/uniQure (Hemgenix&Glybera) Company Details
11.2.2 CSL/uniQure (Hemgenix&Glybera) Business Overview
11.2.3 CSL/uniQure (Hemgenix&Glybera) Hemophilia AAV Gene Therapy Introduction
11.2.4 CSL/uniQure (Hemgenix&Glybera) Revenue in Hemophilia AAV Gene Therapy Business (2021–2026)
11.2.5 CSL/uniQure (Hemgenix&Glybera) Recent Development
11.3 Pfizer
11.3.1 Pfizer Company Details
11.3.2 Pfizer Business Overview
11.3.3 Pfizer Hemophilia AAV Gene Therapy Introduction
11.3.4 Pfizer Revenue in Hemophilia AAV Gene Therapy Business (2021–2026)
11.3.5 Pfizer Recent Development
12 Analyst's Viewpoints/Conclusions
13 Appendix
13.1 Research Methodology
13.1.1 Methodology/Research Approach
13.1.1.1 Research Programs/Design
13.1.1.2 Market Size Estimation
13.1.1.3 Market Breakdown and Data Triangulation
13.1.2 Data Source
13.1.2.1 Secondary Sources
13.1.2.2 Primary Sources
13.2 Author Details
13.3 Disclaimer
List of Tables
Table 1. Global Hemophilia AAV Gene Therapy Market Size Growth Rate by Type (US$ Million): 2021 vs 2025 vs 2032
Table 2. Key Players of AVV5 Vector
Table 3. Key Players of AAVrh74 Vector
Table 4. Global Hemophilia AAV Gene Therapy Market Size Growth by Application (US$ Million): 2021 vs 2025 vs 2032
Table 5. Global Hemophilia AAV Gene Therapy Market Size by Region (US$ Million): 2021 vs 2025 vs 2032
Table 6. Global Hemophilia AAV Gene Therapy Market Size by Region (US$ Million), 2021–2026
Table 7. Global Hemophilia AAV Gene Therapy Market Share by Region (2021–2026)
Table 8. Global Hemophilia AAV Gene Therapy Forecasted Market Size by Region (US$ Million), 2027–2032
Table 9. Global Hemophilia AAV Gene Therapy Market Share by Region (2027–2032)
Table 10. Hemophilia AAV Gene Therapy Market Trends
Table 11. Hemophilia AAV Gene Therapy Market Drivers
Table 12. Hemophilia AAV Gene Therapy Market Challenges
Table 13. Hemophilia AAV Gene Therapy Market Restraints
Table 14. Global Hemophilia AAV Gene Therapy Revenue by Players (US$ Million), 2021–2026
Table 15. Global Hemophilia AAV Gene Therapy Market Share by Players (2021–2026)
Table 16. Global Top Hemophilia AAV Gene Therapy Players by Tier (Tier 1, Tier 2, and Tier 3), based on Hemophilia AAV Gene Therapy Revenue, 2025
Table 17. Ranking of Global Top Hemophilia AAV Gene Therapy Companies by Revenue (US$ Million) in 2025
Table 18. Global 5 Largest Players Market Share by Hemophilia AAV Gene Therapy Revenue (CR5 and HHI), 2021–2026
Table 19. Global Key Players of Hemophilia AAV Gene Therapy, Headquarters and Area Served
Table 20. Global Key Players of Hemophilia AAV Gene Therapy, Products and Applications
Table 21. Global Key Players of Hemophilia AAV Gene Therapy, Date of General Availability (GA)
Table 22. Mergers and Acquisitions, Expansion Plans
Table 23. Global Hemophilia AAV Gene Therapy Market Size by Type (US$ Million), 2021–2026
Table 24. Global Hemophilia AAV Gene Therapy Revenue Market Share by Type (2021–2026)
Table 25. Global Hemophilia AAV Gene Therapy Forecasted Market Size by Type (US$ Million), 2027–2032
Table 26. Global Hemophilia AAV Gene Therapy Revenue Market Share by Type (2027–2032)
Table 27. Global Hemophilia AAV Gene Therapy Market Size by Application (US$ Million), 2021–2026
Table 28. Global Hemophilia AAV Gene Therapy Revenue Market Share by Application (2021–2026)
Table 29. Global Hemophilia AAV Gene Therapy Forecasted Market Size by Application (US$ Million), 2027–2032
Table 30. Global Hemophilia AAV Gene Therapy Revenue Market Share by Application (2027–2032)
Table 31. North America Hemophilia AAV Gene Therapy Market Size Growth Rate by Country (US$ Million): 2021 vs 2025 vs 2032
Table 32. North America Hemophilia AAV Gene Therapy Market Size by Country (US$ Million), 2021–2026
Table 33. North America Hemophilia AAV Gene Therapy Market Size by Country (US$ Million), 2027–2032
Table 34. Europe Hemophilia AAV Gene Therapy Market Size Growth Rate by Country (US$ Million): 2021 vs 2025 vs 2032
Table 35. Europe Hemophilia AAV Gene Therapy Market Size by Country (US$ Million), 2021–2026
Table 36. Europe Hemophilia AAV Gene Therapy Market Size by Country (US$ Million), 2027–2032
Table 37. Asia-Pacific Hemophilia AAV Gene Therapy Market Size Growth Rate by Region (US$ Million): 2021 vs 2025 vs 2032
Table 38. Asia-Pacific Hemophilia AAV Gene Therapy Market Size by Region (US$ Million), 2021–2026
Table 39. Asia-Pacific Hemophilia AAV Gene Therapy Market Size by Region (US$ Million), 2027–2032
Table 40. Latin America Hemophilia AAV Gene Therapy Market Size Growth Rate by Country (US$ Million): 2021 vs 2025 vs 2032
Table 41. Latin America Hemophilia AAV Gene Therapy Market Size by Country (US$ Million), 2021–2026
Table 42. Latin America Hemophilia AAV Gene Therapy Market Size by Country (US$ Million), 2027–2032
Table 43. Middle East & Africa Hemophilia AAV Gene Therapy Market Size Growth Rate by Country (US$ Million): 2021 vs 2025 vs 2032
Table 44. Middle East & Africa Hemophilia AAV Gene Therapy Market Size by Country (US$ Million), 2021–2026
Table 45. Middle East & Africa Hemophilia AAV Gene Therapy Market Size by Country (US$ Million), 2027–2032
Table 46. BioMarin (Roctavian) Company Details
Table 47. BioMarin (Roctavian) Business Overview
Table 48. BioMarin (Roctavian) Hemophilia AAV Gene Therapy Product
Table 49. BioMarin (Roctavian) Revenue in Hemophilia AAV Gene Therapy Business (US$ Million), 2021–2026
Table 50. BioMarin (Roctavian) Recent Development
Table 51. CSL/uniQure (Hemgenix&Glybera) Company Details
Table 52. CSL/uniQure (Hemgenix&Glybera) Business Overview
Table 53. CSL/uniQure (Hemgenix&Glybera) Hemophilia AAV Gene Therapy Product
Table 54. CSL/uniQure (Hemgenix&Glybera) Revenue in Hemophilia AAV Gene Therapy Business (US$ Million), 2021–2026
Table 55. CSL/uniQure (Hemgenix&Glybera) Recent Development
Table 56. Pfizer Company Details
Table 57. Pfizer Business Overview
Table 58. Pfizer Hemophilia AAV Gene Therapy Product
Table 59. Pfizer Revenue in Hemophilia AAV Gene Therapy Business (US$ Million), 2021–2026
Table 60. Pfizer Recent Development
Table 61. Research Programs/Design for This Report
Table 62. Key Data Information from Secondary Sources
Table 63. Key Data Information from Primary Sources
Table 64. Authors List of This Report


List of Figures
Figure 1. Hemophilia AAV Gene Therapy Picture
Figure 2. Global Hemophilia AAV Gene Therapy Market Size Comparison by Type (US$ Million), 2021–2032
Figure 3. Global Hemophilia AAV Gene Therapy Market Share by Type: 2025 vs 2032
Figure 4. AVV5 Vector Features
Figure 5. AAVrh74 Vector Features
Figure 6. Global Hemophilia AAV Gene Therapy Market Size by Application (US$ Million), 2021–2032
Figure 7. Global Hemophilia AAV Gene Therapy Market Share by Application: 2025 vs 2032
Figure 8. Hemophilia A Case Studies
Figure 9. Hemophilia B Case Studies
Figure 10. Hemophilia AAV Gene Therapy Report Years Considered
Figure 11. Global Hemophilia AAV Gene Therapy Market Size (US$ Million), Year-over-Year: 2021–2032
Figure 12. Global Hemophilia AAV Gene Therapy Market Size, (US$ Million), 2021 vs 2025 vs 2032
Figure 13. Global Hemophilia AAV Gene Therapy Market Share by Region: 2025 vs 2032
Figure 14. Global Hemophilia AAV Gene Therapy Market Share by Players in 2025
Figure 15. Global Hemophilia AAV Gene Therapy Market Share by Company Type (Tier 1, Tier 2, and Tier 3)
Figure 16. The Top 10 and 5 Players Market Share by Hemophilia AAV Gene Therapy Revenue in 2025
Figure 17. North America Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 18. North America Hemophilia AAV Gene Therapy Market Share by Country (2021–2032)
Figure 19. United States Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 20. Canada Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 21. Europe Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 22. Europe Hemophilia AAV Gene Therapy Market Share by Country (2021–2032)
Figure 23. Germany Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 24. France Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 25. U.K. Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 26. Italy Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 27. Russia Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 28. Ireland Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 29. Asia-Pacific Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 30. Asia-Pacific Hemophilia AAV Gene Therapy Market Share by Region (2021–2032)
Figure 31. China Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 32. Japan Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 33. South Korea Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 34. Southeast Asia Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 35. India Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 36. Australia & New Zealand Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 37. Latin America Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 38. Latin America Hemophilia AAV Gene Therapy Market Share by Country (2021–2032)
Figure 39. Mexico Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 40. Brazil Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 41. Middle East & Africa Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 42. Middle East & Africa Hemophilia AAV Gene Therapy Market Share by Country (2021–2032)
Figure 43. Israel Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 44. Saudi Arabia Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 45. UAE Hemophilia AAV Gene Therapy Market Size YoY Growth (US$ Million), 2021–2032
Figure 46. BioMarin (Roctavian) Revenue Growth Rate in Hemophilia AAV Gene Therapy Business (2021–2026)
Figure 47. CSL/uniQure (Hemgenix&Glybera) Revenue Growth Rate in Hemophilia AAV Gene Therapy Business (2021–2026)
Figure 48. Pfizer Revenue Growth Rate in Hemophilia AAV Gene Therapy Business (2021–2026)
Figure 49. Bottom-up and Top-down Approaches for This Report
Figure 50. Data Triangulation
Figure 51. Key Executives Interviewed
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